CNS 2020 presentation Distinguishing pediatric movement disorders Uncovering aromatic L-amino acid decarboxylase (AADC) deficiency
CNS 2020 Infographic Distinguishing pediatric movement disorders Uncovering aromatic L-amino acid decarboxylase (AADC) deficiency
CNS 2020 presentation: Distinguishing pediatric movement disorders: Uncovering aromatic L-amino acid decarboxylase (AADC) deficiency
ASGCT 2020 poster: Motor function in children with aromatic L-amino acid decarboxylase (AADC) deficiency treated with eladocagene exuparvovec: compassionate use study
ASGCT 2020 poster: Motor function in children with aromatic L-amino acid decarboxylase (AADC) deficiency treated with eladocagene exuparvovec: Interim findings from a phase 1/2 study
ASGCT 2020 Infographic: From bench to bedside: Uncovering the potential of gene therapy
CNS 2019 poster: Safety and efficacy outcomes in children with aromatic L-amino acid decarboxylase (AADC) deficiency treated with eladocagene exuparvovec gene therapy: Results from three clinical trials
CNS 2020 Infographic: Distinguishing pediatric movement disorders: Uncovering aromatic L-amino acid decarboxylase (AADC) deficiency