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Society for the Study of Inborn Errors of Metabolism (SSIEM)

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The Society for the Study of Inborn Errors of Metabolism (SSIEM) Annual Symposium is a yearly conference bringing together clinicians and scientists to discuss the challenges and opportunities in the field of inborn errors of metabolism.

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Society for the Study of Inborn Errors of Metabolism (SSIEM)
SSIEM 2022 poster: A two-part, international, real-world, observational registry of participants diagnosed with aromatic L-amino acid decarboxylase deficiency (AADC-d) with or without treatment with eladocagene exuparvovec
This poster, presented at SSIEM 2022, provides an overview of the AADCAware registry, which has been designed to improve understanding of AADC deficiency diagnosis, disease progression and standard of care
Year
Therapy area
Type
Congress
US-AADC-0455 | June 2023
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US-CORP-0330 | July 2022

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