Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Congress activities | Muscular Dystrophy Association (MDA) Annual Clinical & Scientific Conference | MDA 2022 poster: Pulmonary function in patients with Duchenne muscular dystrophy from the STRIDE Registry and CINRG Natural History Study: A matched cohort analysis

MDA 2022 poster: Pulmonary function in patients with Duchenne muscular dystrophy from the STRIDE Registry and CINRG Natural History Study: A matched cohort analysis

This poster, presented at the 2022 MDA Conference in Nashville, Tennessee, USA, shows results from a propensity score-matched registry analysis, using data from the STRIDE Registry and CINRG Natural History Study, to determine the effect of a mutation-specific treatment for nonsense mutation Duchenne muscular dystrophy (nmDMD) on pulmonary function

  • Find out about the demographics of patients in the STRIDE Registry and CINRG Natural History Study who were propensity score-matched to evaluate the effect of a treatment for nmDMD on pulmonary function
  • Compare results from 2 cohorts of patients (N=241 in each) who received either a mutation-specific treatment for nmDMD plus standard of care (SoC), or SoC alone
  • Review the pulmonary function outcome, as measured by ages at percent predicted forced vital capacity, for each cohort
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US-DMD-0282 I December 2023
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