Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Publications | Publication: Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD): Patient demographics and characteristics from the STRIDE Registry

Publication: Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD): Patient demographics and characteristics from the STRIDE Registry

This research article, published in the Journal of Comparative Effectiveness Research, outlines the initial demographics and baseline characteristics of patients enrolled in STRIDE, an observational registry of nmDMD patients receiving a mutation-specific DMD therapy

  • The demographics and baseline characteristics of the Strategic Targeting of Registries and International Database of Excellence (STRIDE) Registry population and the principal interim safety results (data cut-off: 9 July 2018) is presented

Muntoni F, Desguerre I, Guglieri M, et al. J Comp Eff Res. 2019;8(14):1187–1200

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