Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Congress activities | Academy of Managed Care Pharmacy (AMCP) | AMCP 2021 poster: Disease progression indicators in Duchenne muscular dystrophy (DMD) for use in matched analyses comparing treatment effects: A targeted literature review

AMCP 2021 poster: Disease progression indicators in Duchenne muscular dystrophy (DMD) for use in matched analyses comparing treatment effects: A targeted literature review

This poster, presented at the 2021 virtual AMCP Annual Meeting, describes a literature review to establish core prognostic indicators for DMD, to help inform propensity score-matching models in studies

  • Review the search strategy of a targeted literature review including 256 publications
  • Understand the levels of evidence of prognostic indicators, including patient age, glucocorticoid exposure, cardiac, respiratory and bone health, limb function, and age at loss of ambulation
  • Explore the core prognostic indicators for use in future non-randomized propensity score-matched studies investigating treatments for DMD
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MED-ALL-DMD-2200031 | march 2022
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