ICNMD 2021 poster: Ataluren delays loss of ambulation (LoA) and decline in pulmonary function in patients with nonsense mutation Duchenne muscular dystrophy (DMD)

This poster, presented at the ICNMD virtual meeting in 2021, shows the results from a study evaluating efficacy of a mutation-specific DMD therapy

  • Review the background, methods, and clinical characteristics of patients involved in a propensity score-matched study to evaluate the efficacy of a mutation-specific for DMD
  • Explore the Kaplan-Meier analysis of age at LoA for patients treated with a mutation-specific DMD therapy + standard of care (SoC) vs SoC alone
  • Review the comparison of age at milestones of pulmonary function decline in the 2 treatment populations

▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The European Summary of Product Characteristics for ataluren is available here. Please refer to your local country guidance for more information.

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MED-ALL-DMD-2200031 | March 2022
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