MDA 2021 poster: Disease progression indicators in Duchenne muscular dystrophy (DMD) for use in matched analyses comparing treatment effects: A targeted literature review

This poster, presented at the 2021 virtual MDA Conference, presents findings from a literature review to determine core prognostic indicators for DMD, to help inform propensity score-matching models in studies

  • Learn about the search strategy of a targeted literature review including 256 publications
  • Review the levels of evidence for prognostic indicators, including patient age, glucocorticoid exposure, cardiac, respiratory and bone health, limb function, and age at loss of ambulation
  • Understand the potential core prognostic indicators for use in future non-randomized propensity score-matched studies investigating treatments for DMD
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MED-ALL-DMD-2200031 | March 2022
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