WMS 2021 poster: Comparison of North Star Ambulatory Assessment score change in nonsense mutation Duchenne muscular dystrophy patients receiving ataluren: STRIDE Registry vs Phase 3 clinical trial
This poster, presented at the 2021 virtual WMS Annual Congress, presents a comparison of ambulatory outcomes following treatment for nonsense mutation Duchenne muscular dystrophy (nmDMD) in a registry study and a Phase 3 clinical trial
Review the demographics and baseline characteristics of patients with nmDMD from the 2 study populations
Discover the results obtained from analysis of the STRIDE Registry of real-world data compared with those of Study 020 – a randomized, double-blind, placebo-controlled Phase 3 clinical trial
Learn about the changes in total North Star Ambulatory Assessment (NSAA) score and individual ambulatory function assessment items over a 5-year follow-up period
▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC at firstname.lastname@example.org.
Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The European Summary of Product Characteristics for ataluren is available here. Please refer to your local country guidance for more information.
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MED-ALL-DMD-2200031 | March 2022
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