During this case study, you will discover the diagnostic journey of Oliver* and review possible diagnostic choices with related feedback
The role of propensity score matching (PSM) in statistical analysis of effectiveness in medical research is described in this animation
The genetic basis of DMD and the role of genetic testing for diagnosis of the condition are presented in this PTC Therapeutics-sponsored webinar from 2021.
This presentation, from a PTC Therapeutics-sponsored webinar, discusses the approach of clinical trials in the field of DMD
This webinar from a PTC Therapeutics-sponsored meeting discusses the transition of children with DMD from pediatric to adult care
This expert-led webinar from a PTC Therapeutics-sponsored meeting provides an update on the scientific approaches to the treatment of Duchenne muscular dystrophy (DMD), with specific reference to nonsense readthrough agents
This expert-led webinar from a PTC Therapeutics-sponsored meeting provides an overview of the common emotional and behavioral symptoms observed in children with DMD
This webinar from a PTC Therapeutics-sponsored meeting in 2020 discusses the complexity of DMD management and describes the current approaches for clinical management with a clinical case study
This expert-led webinar from 2020 discusses the genetics of DMD and describes the consequences of different mutations, the key steps for achieving a diagnosis, and the importance of an early genetic diagnosis
The signs and symptoms of DMD are presented and the steps to diagnosis are discussed in this PTC Therapeutics-sponsored webinar from 2020
This presentation of the psychological effects of DMD and Becker muscular dystrophy (BMD) featured during a PTC Therapeutics-sponsored standalone meeting in 2021
This webinar from 2021 explores the mitochondrial mechanisms behind DMD and other dystrophinopathies and the potential role in future treatment approaches
View our presentation given at a webinar in 2021 which discusses the role of corticosteroids in the management of inflammation in patients with DMD
View our presentation delivered at the US virtual expert masterclass which discusses the genetics and efficacy of clinical management interventions of DMD (November 2020)
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Clinical insights into topics such as the mutational spectrum and disease continuum of DMD, best practice for obtaining a mutation-specific diagnosis, and the role of treatment in DMD management.