Publication: Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis

This research article, published in PLoS ONE, provides a summary of the prognostic indicators of disease progression in Duchenne muscular dystrophy (DMD)

  • Understand the approach taken to systematically review the available data to determine prognostic indicators of disease progression in DMD
  • Review the wealth of data available for each prognostic indicator
  • Learn which prognostic indicators are considered ‘core’ with regard to determining disease progression outcomes in DMD

Ferizovic N, Summers J, Zárate IBO, et al. PLoS ONE. 2022;17(3):e0265879

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US-DMD-0299 | March 2023
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