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Home | Central nervous system | Aromatic L-amino acid decarboxylase (AADC) deficiency | Publications | Publication: A discrete choice experiment to derive health utilities for aromatic L-amino acid decarboxylase (AADC) deficiency in France

Publication: A discrete choice experiment to derive health utilities for aromatic L-amino acid decarboxylase (AADC) deficiency in France

This research article, published in Patient Related Outcome Measures, provides results from a discrete choice experiment to determine health utility values for AADC deficiency, carried out using a sample of the general population in France

  • Find out more about the methodology used to select a representative sample of the general French population for this study
  • Review the health utilities for AADC deficiency syndromes derived from this analysis
  • Understand more about the perceived impact of the different symptoms of AADC deficiency, and how this is affected by disease progression
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MED-US-CORP-2500008 | November 2025

Smith AB, Hanbury A, Whitty JA, et al. Patient Relat Outcome Meas. 2022;13:21–30

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MED-US-CORP-2600009 | September 2026

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MED-US-AADC-2600008 | February 2026

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