Publication: Pharmacodynamics, efficacy, and safety of intraputaminal eladocagene exuparvovec administered to pediatric patients with aromatic L-amino acid decarboxylase deficiency using an MR-compatible cannula: 48 weeks of follow-up
This research article explores the administration of eladocagene exuparvovec using the SmartFlow magnetic resonance (MR)-compatible ventricular cannular in pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency
- Review the pathophysiology of AADC deficiency, a rare neurotransmitter-related disease
- Learn about the SmartFlow MR-compatible ventricular cannular for intraputaminal administration
- Assess the pharmacodynamics, efficacy and safety of eladocagene exuparvovec using the SmartFlow MR-compatible ventricular cannular in this population
MED-US-CORP-2500008 | November 2025
Curry DJ, Pearl PL, Stone SSD, et al. J Inherit Metab Dis. 2026;49(2);e70151.
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MED-US-CORP-2600001 | February 2026
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