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GMDI 2026 supporting infographic: Effect of long-term sepiapterin treatment on dietary phenylalanine tolerance in participants with phenylketonuria aged less than or equal to 2 years: The APHENITY extension study

This infographic, which supports the poster presented at GMDI 2026, highlights findings from the APHENITY extension study evaluating the long-term effects of sepiapterin treatment on dietary phenylalanine tolerance in children aged ≤2 years with phenylketonuria (PKU)

  • Learn more about the long-term tolerability of sepiapterin in young children with PKU
  • Review extension study results demonstrating changes in natural protein intake, blood phenylalanine levels, and overall treatment response among participants continuing therapy
  • Understand the potential of sepiapterin to improve dietary phenylalanine tolerance and support more liberalized dietary management in early childhood

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MED-US-CORP-2600009 | September 2026

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