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Home | Metabolism | Phenylketonuria (PKU) | Congress activities | Society for Inherited Metabolic Disorders (SIMD) | SIMD 2026 Symposium: From clinical trials to clinical practice: Exploring the role of sepiapterin PKU management

SIMD 2026 Symposium: From clinical trials to clinical practice: Exploring the role of sepiapterin PKU management

This symposium, presented at SIMD 2026, reviews the latest clinical trial and real-world evidence of sepiapterin across a broad spectrum of patients with phenylketonuria (PKU)

  • Review evidence from clinical trials and real-world case studies of sepiapterin treatment across a broad spectrum of patients with PKU
  • Understand the role of early sepiapterin initiation in pediatric patients
  • Gain insights from a live Q&A with the panel, discussing administration, individualised goals and disease management
Always consult the prescribing information before prescribing any products

MED-US-CORP-2500008 | November 2025

​​This symposium was developed and funded by PTC Therapeutics for SIMD 2026.​

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