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Home | Metabolism | Phenylketonuria (PKU) | Congress activities | The Society for the Study of Inborn Errors of Metabolism (SSIEM) | SSIEM 2026 poster: Dietary liberalization in patients with PKU and controlled blood phenylalanine levels: APHENITY extension study findings

SSIEM 2026 poster: Dietary liberalization in patients with PKU and controlled blood phenylalanine levels: APHENITY extension study findings

This poster, presented at SSIEM 2026, examines the long-term efficacy and safety of sepiapterin in people with phenylketonuria (PKU) and controlled blood phenylalanine (Phe) levels

  • Review data highlighting the effects of sepiapterin in participants with PKU who have controlled blood Phe levels (<360 μmol/l)
  • Assess changes in low-Phe supplemental protein intake and the proportion of participants meeting dietary protein targets
  • Understand the safety and tolerability of long-term sepiapterin treatment and its potential to support greater dietary flexibility
Always consult the prescribing information before prescribing any products

MED-US-CORP-2500008 | November 2025

​​This poster was developed and funded by PTC Therapeutics for SSIEM 2026.​

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