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Home | Metabolism | Phenylketonuria (PKU) | Congress activities | The Society for the Study of Inborn Errors of Metabolism (SSIEM) | SSIEM 2026 poster: Efficacy and safety of sepiapterin in individuals with PKU and baseline phenylalanine levels equal to or more than 900 μmol/l

SSIEM 2026 poster: Efficacy and safety of sepiapterin in individuals with PKU and baseline phenylalanine levels equal to or more than 900 μmol/l

This poster, presented at SSIEM 2026, examines the efficacy and safety of sepiapterin in individuals with phenylketonuria (PKU) and baseline phenylalanine (Phe) levels ≥900 µmol/L, including its impact on blood Phe levels and dietary protein tolerance

  • Review sepiapterin response rates in participants with high baseline Phe levels in three key studies
  • Gain insights into the proportion of participants achieving clinically meaningful reductions in blood Phe
  • Understand the safety profile of sepiapterin, and the potential for greater dietary flexibility for people living with PKU
Always consult the prescribing information before prescribing any products

MED-US-CORP-2500008 | November 2025

​​This poster was developed and funded by PTC Therapeutics for SSIEM 2026.​

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