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Home | Central nervous system | Aromatic L-amino acid decarboxylase (AADC) deficiency | Congress activities | The American College of Medical Genetics (ACMG)

The American College of Medical Genetics (ACMG)

The American College of Medical Genetics (ACMG) brings together medical genetics professionals and industry leaders to discuss the latest discoveries and best practice in genetic disorders, rare diseases, genome sequencing, gene therapies and genetic counseling.

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The American College of Medical Genetics (ACMG)
ACMG 2025 oral presentation: Administration of eladocagene exuparvovec using the SmartFlow magnetic resonance-compatible ventricular cannula in pediatric patients with aromatic L-amino acid decarboxylase deficiency
This oral presentation, presented at ACMG 2025, assesses the pharmacodynamics of eladocagene exuparvovec using the SmartFlow magnetic resonance (MR)-compatible ventricular cannula in pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency
Always consult the prescribing information before prescribing any products

MED-US-CORP-2500008 | November 2025

MED-US-AADC-2600002 | February 2026

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