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International congresses, conferences and meetings offer the opportunity to share data and drive discussion that can progress the management of conditions such as aromatic L-amino acid decarboxylase (AADC) deficiency. Access our content from recent congresses and society meetings here.

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This poster, presented at ISPMD 2024, explores the administration of eladocagene exuparvovec using the SmartFlow magnetic resonance (MR)-compatible ventricular cannular in pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency
This poster, presented at NSGC 2023, provides an overview of the utilization of artificial intelligence in analyzing Electronic Health Record (EHR) data to identify patients who may be at increased risk of aromatic L-amino acid decarboxylase (AADC) deficiency, with the aim of decreasing diagnostic delay for patients
Therapy area

Access PTC abstracts, infographics, posters and symposia, presented at international meetings in the fields of pediatric neurology, cognitive neuroscience, and neuromuscular disorders, such as the Child Neurological Society (CNS) Annual Meeting, American Society of Gene and Cell Therapy (ASGCT) General Meeting and the International Symposium on Genetic Syndromes with Movement Disorders and Epilepsy (GSMDE).

MED-ALL-AADC-2200032 | September 2023
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MED-ALL-CORP-2200029 | October 2023


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