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International congresses, conferences and meetings offer the opportunity to share data and drive discussion that can progress the management of conditions such as aromatic L-amino acid decarboxylase (AADC) deficiency. Access our content from recent congresses and society meetings here.

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This poster, presented at SSIEM 2022, provides an overview of the AADCAware registry, which has been designed to improve understanding of AADC deficiency diagnosis, disease progression and standard of care
Change in the duration and frequency of oculogyric crises (OGC) in children with AADC deficiency following treatment with eladocagene exuparvovec, an investigational gene therapy, are presented in this poster from the 2021 CNS Annual Meeting 
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Access PTC abstracts, infographics, posters and symposia, presented at international meetings in the fields of pediatric neurology, cognitive neuroscience, and neuromuscular disorders, such as the Child Neurological Society (CNS) Annual Meeting, the American Academy of Neurology (AAN) Annual Meeting, American Society of Gene and Cell Therapy (ASGCT) General Meeting and the International Symposium on Genetic Syndromes with Movement Disorders and Epilepsy (GSMDE).

MED-ALL-AADC-2200032 | March 2022
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