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Browse selected scientific articles published in journals across the fields of molecular genetics, metabolism, and neurology to facilitate your understanding of the spectrum, molecular and genetic basis, and management of Duchenne muscular dystrophy (DMD)

Please select a publication review of interest below:

Published in the Journal of Neurology, this is an updated interim report from the ongoing Strategic Targeting of Registries and International Database of Excellence (STRIDE) international, multicenter registry of real-world ataluren use in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD)

Learn more about our phase I–III clinical trials, patient registries and natural history studies in DMD.

MED-ALL-DMD-2100127 | February 2024
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This educational website provides you with the latest scientific data and expert
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MED-ALL-CORP-2200029 | October 2023


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