The American College of Medical Genetics (ACMG)
The American College of Medical Genetics (ACMG) brings together medical genetics professionals and industry leaders to discuss the latest discoveries and best practice in genetic disorders, rare diseases, genome sequencing, gene therapies and genetic counseling.
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Eladocagene Exuparvovec is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.
MED-ALL-PTC-AADC-2500006 | September 2025