SIMD 2024 poster: Efficacy and safety of oral sepiapterin in participants with phenylketonuria on sapropterin dihydrochloride at time of Phase 3 APHENITY study entry
This poster, presented at SIMD 2024, evaluates the efficacy and safety data of sepiapterin vs placebo in patients with phenylketonuria (PKU) who were receiving sapropterin dihydrochloride at the time of APHENITY study entry
Learn more about sepiapterin, an investigational oral treatment for PKU
Review the efficacy results of oral sepiapterin in a subset of PKU patients who were receiving sapropterin dihydrochloride at study entry
Understand the safety profile of sepiapterin in this subset of participants
Sepiapterin is an investigational product and is not currently approved in any country.
This poster was developed and funded by PTC Therapeutics for SIMD 2024.
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MED-ALL-PKU-2400094 | May 2024
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