SIMD 2024 poster: Preliminary results from the ongoing APHENITY extension study: Sepiapterin reduces blood Phe with improved dietary Phe tolerance in participants with phenylketonuria

This poster, presented at SIMD 2024, discusses the preliminary results from the ongoing APHENITY extension study, which evaluates the safety of sepiapterin and its effect on dietary phenylalanine (Phe) consumption in participants with phenylketonuria (PKU)

  • Understand the preliminary results from the APHENITY extension study
  • Review the effect of sepiapterin on dietary Phe consumption in participants who completed the Phase 3 APHENITY trial and participated in the Phe tolerance assessment during the APHENITY extension study
  • Read more about the safety profile of sepiapterin in this ongoing study

Sepiapterin is an investigational product and is not currently approved in any country.

This poster was developed and funded by PTC Therapeutics for SIMD 2024.

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MED-ALL-PKU-2400094 | May 2024
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