SSIEM 2023 symposium: Advancing the treatment of PKU: Results of the Phase 3 APHENITY trial

This symposium at SSIEM 2023 discussed the results of the Phase 3 APHENITY trial, investigating the safety and efficacy of sepiapterin in patients with phenylketonuria (PKU)

  • Learn more about sepiapterin, an investigational treatment for PKU
  • Explore key efficacy results, which assessed reduction in blood phenylalanine levels
  • Review the safety and tolerability of sepiapterin
  • Discover the open-label extension study, including the study protocol and its preliminary results

Sepiapterin is an investigational product currently in development for PKU.

This symposium was developed and funded by PTC Therapeutics for SSIEM 2023.

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MED-ALL-PKU-2300099 | October 2023
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