ICNMD 2020 virtual symposium: Advancing the management of Duchenne muscular dystrophy (DMD): The role of real-world evidence

Watch our virtual symposium at ICNMD 2020, which discusses long-term real-world evidence (RWE) regarding ataluren use in patients with nonsense mutation DMD (nmDMD)

  • Review the diagnostic and testing information used to make an accurate genetic diagnosis of DMD
  • RWE for determining treatment effect in patients with DMD and informing the future management of these patients is discussed
  • View the latest RWE for a mutation-specific DMD therapy for patients with nmDMD in clinical practice

This is a virtual symposium hosted by PTC at ICNMDigital 2020 and was organized and funded by PTC Therapeutics. This presentation was approved by the Scientific Program Committee as an independent activity held in conjunction with ICNMDigital. This presentation was not sponsored or endorsed by ICNMDigital.

This symposium recording has been chapterized to enable ease of viewing.

 

Register now to unlock the content

Register now to access the content on this page

Already registered?
If not, register below

Registration
  • This Website is intended only for healthcare professionals (“Website“), is operated by PTC Therapeutics. (together with its affiliates “PTC”). In order to access the restricted content on this Website:

    *
    *
  • PTC will delete immediately the information provided if we cannot confirm you are healthcare professional.
    Otherwise, in case of successful verification, PTC will retain the information provided for a period of two (2) years two (2) years following your registration (i) only for the purposes of providing you access to this Website; and/or (ii) in case you signed up to receive PTC updates.

Providing your personal data and your consent is voluntary, and you have the right to withdraw your consent at any time, without giving any reasons. Please consult our Privacy Statement for more information on the processing of your personal data.
For any enquiry relating to the processing of your personal data or if you want to exercise your privacy related rights or withdraw your consent, you can contact PTC’s Privacy Office at: Dataprivacy@ptcbio.com.

You can unsubscribe from updates at any time when receiving an email from PTC.

GL-DMD-0312 | June 2021
Sign in or register to access exclusive content on this site 
  REGISTER

Welcome to MEDhub

A website for healthcare professionals, provided by PTC Therapeutics

This educational website provides you with the latest scientific data and expert
insights on the diagnosis and management of a range of rare diseases across the neuromuscular system, central nervous system, and other areas

This content is protected. To view it please enter your email address below:

Register here to access the content on the site
GL-CORP-0207 | June 2021

COMING SOON

The content you are trying to access is not currently available.

We will be updating the MEDhub site regularly to provide you with up-to-date, insightful expert-led content. To be notified when new additions become available, register now.