Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Congress activities | International Congress on Neuromuscular Diseases (ICNMD) | ICNMD 2020 virtual symposium: Advancing the management of Duchenne muscular dystrophy (DMD): The role of real-world evidence

ICNMD 2020 virtual symposium: Advancing the management of Duchenne muscular dystrophy (DMD): The role of real-world evidence

Watch our virtual symposium at ICNMD 2020, which discusses long-term real-world evidence (RWE) regarding ataluren use in patients with nonsense mutation DMD (nmDMD)

  • Review the diagnostic and testing information used to make an accurate genetic diagnosis of DMD
  • RWE for determining treatment effect in patients with DMD and informing the future management of these patients is discussed
  • View the latest RWE for a mutation-specific DMD therapy for patients with nmDMD in clinical practice

This is a virtual symposium hosted by PTC at ICNMDigital 2020 and was organized and funded by PTC Therapeutics. This presentation was approved by the Scientific Program Committee as an independent activity held in conjunction with ICNMDigital. This presentation was not sponsored or endorsed by ICNMDigital.

This symposium recording has been chapterized to enable ease of viewing.

 

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