MDA 2024 poster: Characterization of deflazacort use in young Duchenne muscular dystrophy patients: An analysis of data from the PTC Cares database

This poster, presented at MDA 2024, provides insights into the demographics of young patients with Duchenne muscular dystrophy (DMD) who are receiving deflazacort in the US

  • Learn more about deflazacort use in patients ≥2 years of age
  • Explore the unmet need in referral rates for young patients with DMD
  • Review the characteristics of young patients receiving deflazacort

Deflazacort is a corticosteroid indicated for the treatment of DMD in patients 2 years of age and older. PTC Therapeutics is the Marketing Authorization Holder for deflazacort in the US only. Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The US Prescribing Information for deflazacort is available here. Please refer to your local country guidance for more information.

For medical information, product complaints, or to report an adverse event, please call 1-866-562-4620 or email at usmedinfo@ptcbio.com. You may also report adverse events directly to FDA at 1-800-FDA-1088 or www.fda.gov/medwatch.

This poster was developed and funded by PTC Therapeutics for MDA 2024.

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MED-ALL-DMD-2400003 | March 2024
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