Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Congress activities | World Muscle Society (WMS) Annual Congress | WMS 2023 poster: Pulmonary function in patients with Duchenne muscular dystrophy from the STRIDE Registry and the CINRG Natural History Study: A matched cohort analysis

WMS 2023 poster: Pulmonary function in patients with Duchenne muscular dystrophy from the STRIDE Registry and the CINRG Natural History Study: A matched cohort analysis

This poster, presented at WMS 2023, provides results of a propensity score-matched registry analysis, using data from the STRIDE Registry and CINRG Natural History Study, to assess the effect of mutation-specific treatment for nonsense mutation Duchenne muscular dystrophy (nmDMD) on pulmonary function

  • Explore the patient demographics for the STRIDE Registry and CINRG Natural History Study
  • Compare results from 2 groups of patients who received either a mutation-specific treatment for nmDMD plus standard of care (SoC), or SoC alone
  • Discover the outcomes of pulmonary functioning for each patient group, measured by age at <60% and <50% predicted forced vital capacity

▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The European Summary of Product Characteristics for ataluren is available here. Please refer to your local country guidance for more information.

This poster was developed and funded by PTC Therapeutics for WMS 2023.

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