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All congress activities

International congresses, conferences and meetings offer the opportunity to share data and drive discussion that can progress the management of conditions such as aromatic L-amino acid decarboxylase (AADC) deficiency. Access our content from recent congresses and society meetings here.

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This oral presentation, presented at ACMG 2025, assesses the pharmacodynamics of eladocagene exuparvovec using the SmartFlow magnetic resonance (MR)-compatible ventricular cannula in pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency
This poster, presented at ISPMD 2024, explores the administration of eladocagene exuparvovec using the SmartFlow magnetic resonance (MR)-compatible ventricular cannular in pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency

Access PTC abstracts, infographics, posters and symposia, presented at international meetings in the fields of pediatric neurology, cognitive neuroscience, and neuromuscular disorders, such as the American Academy of Neurology (AAN), Child Neurological Society (CNS) Annual Meeting and the European Society of Gene and Cell Therapy (ESGCT).

MED-ALL-AADC-2200032 | June 2025

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© 2025 PTC Therapeutics. All rights reserved | MED-ALL-CORP-2200029 | June 2025

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MED-ALL-CORP-2200029 | June 2025

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