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ISPMD 2024 poster: Pharmacodynamics of eladocagene exuparvovec and safety of the SmartFlow magnetic resonance-compatible ventricular cannula for administering eladocagene exuparvovec in paediatric participants

This poster, presented at ISPMD 2024, explores the administration of eladocagene exuparvovec using the SmartFlow magnetic resonance (MR)-compatible ventricular cannular in pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency

  • Review the pathophysiology of AADC deficiency, a rare neurotransmitter-related disease
  • Learn about the SmartFlow MR-compatible ventricular cannular for intraputaminal administration
  • Assess the pharmacodynamics and safety of eladocagene exuparvovec using the SmartFlow MR-compatible ventricular cannular in pediatric patients with AADC deficiency

This poster was developed and funded by PTC Therapeutics for ISPMD 2024.

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MED-ALL-AADC-2400001 | June 2025

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