ISPMD 2024 poster: Pharmacodynamics of eladocagene exuparvovec and safety of the SmartFlow magnetic resonance-compatible ventricular cannula for administering eladocagene exuparvovec in paediatric participants
This poster, presented at ISPMD 2024, explores the administration of eladocagene exuparvovec using the SmartFlow magnetic resonance (MR)-compatible ventricular cannular in pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency
- Review the pathophysiology of AADC deficiency, a rare neurotransmitter-related disease
- Learn about the SmartFlow MR-compatible ventricular cannular for intraputaminal administration
- Assess the pharmacodynamics and safety of eladocagene exuparvovec using the SmartFlow MR-compatible ventricular cannular in pediatric patients with AADC deficiency
Eladocagene Exuparvovec is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.
MED-ALL-PTC-AADC-2500006 | September 2025
This poster was developed and funded by PTC Therapeutics for ISPMD 2024.
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