Home | Central Nervous System | Aromatic L-amino acid decarboxylase (AADC) deficiency | Publications | Publication: Eliciting health state utilities for aromatic L-amino acid decarboxylase (AADC) deficiency: A UK vignette study

Publication: Eliciting health state utilities for aromatic L-amino acid decarboxylase (AADC) deficiency: A UK vignette study

This research article, published in Journal of Patient-Reported Outcomes, presents a novel approach to evaluating the impact of AADC deficiency on health-related quality of life

  • This is the first study to derive health-state utilities for AADC deficiency
  • Understand how hypothetical health-state vignettes, and participants who imagine themselves as the parent or caregiver of a child with AADC deficiency, were used to develop health-state utilities
  • Recognize the role of health-state utilities in economic modelling to investigate the cost-effectiveness of AADC deficiency treatments

Smith AB, et al. J Patient Rep Outcomes. 2021;5:130.

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