Publication: Eliciting health state utilities for aromatic L-amino acid decarboxylase (AADC) deficiency: A vignette study in France

This research article, published in Journal of Patient-Reported Outcome Measures, presents an approach specific to France that evaluates the impact of AADC deficiency on health-related quality of life

  • Learn about the development of France-specific health-state utilities for AADC deficiency
  • Understand how hypothetical health-state vignettes, developed using participants who imagine themselves as the parent or caregiver of a child with AADC deficiency, were used to develop health-state utilities
  • Recognize the potential importance of these health-state utilities in economic modelling to investigate the cost-effectiveness of AADC deficiency treatment

Smith AB, et al. Patient Relat Outcome Meas. 2021;12 237–246

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MED-ALL-AADC-2200023 | March 2022
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