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Home | Central nervous system | Friedreich’s ataxia | Publications | Publication: Clinical evidence of interventions assessed in Friedreich ataxia: A systematic review

Publication: Clinical evidence of interventions assessed in Friedreich ataxia: A systematic review

This systematic literature review, published in Therapeutic Advances in Rare Disease, discusses the therapeutic landscape in Friedreich’s ataxia. The review also identifies a considerable unmet need for patients with Friedreich’s ataxia

  • Understand the management approach for this rare progressive neurodegenerative genetic condition
  • Review the published evidence and the current treatment landscape for Friedreich’s ataxia
  • Find out why further research into effective treatments that slow or reverse the damage in patients is important
  • Learn more about the unmet treatment need in Friedreich’s ataxia

Jain P, et al. Ther Adv Rare Dis. 2022;3:26330040221139872

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