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Home | Metabolism | Phenylketonuria (PKU) | Congress activities | Society for Inherited Metabolic Disorders (SIMD) | SIMD 2026 Symposium: From clinical trials to clinical practice: Exploring the role of sepiapterin PKU management

SIMD 2026 Symposium: From clinical trials to clinical practice: Exploring the role of sepiapterin PKU management

This symposium, presented at SIMD 2026, reviews the latest clinical trial and real-world evidence of sepiapterin across a broad spectrum of people with phenylketonuria (PKU)

  • Review evidence from clinical trials and real-world case studies of sepiapterin treatment across a broad spectrum of people with PKU
  • Understand the role of early sepiapterin initiation in pediatric patients
  • Gain insights from a live Q&A with the panel, discussing administration, individualised goals and disease management
▼ Sepiapterin is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.

MED-ALL-PTC923-2500012 | September 2025

​​This symposium was developed and funded by PTC Therapeutics for SIMD 2026.​

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MED-ALL-PKU-2600159 | August 2026

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