GMDI 2024 poster: APHENITY extension study dietary Phe Tolerance Assessment design using 3-day diet records: An interim report

This poster, presented at GMDI 2024, describes the APHENITY extension study phenylalanine (Phe) tolerance assessment design and reports on the compliance rate for 3-day diet diaries among participants

  • Learn more about sepiapterin, an investigational oral treatment for phenylketonuria (PKU)
  • Review the APHENITY extension study and its primary endpoints
  • Understand the compliance rates in using a 3-day diet diary to assess Phe tolerance changes in individuals with PKU treated with sepiapterin

Sepiapterin is an investigational product and is not currently approved in any country.

This poster was developed and funded by PTC Therapeutics for GMDI 2024.

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MED-ALL-PKU-2400096 | April 2024
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