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Home | Metabolism | Phenylketonuria (PKU) | Congress activities | The Society for the Study of Inborn Errors of Metabolism (SSIEM) | SSIEM 2024 symposium: Unlocking new possibilities in phenylketonuria

SSIEM 2024 symposium: Unlocking new possibilities in phenylketonuria

This symposium, presented at SSEIM 2024, provides an overview of sepiapterin as a potential treatment for phenylketonuria (PKU) and its implications for patient management

  • Recognize the unmet needs in PKU and how patient care is managed
  • Learn more about sepiapterin as a potential treatment for PKU
  • Understand the mechanism of action of sepiapterin
▼ Sepiapterin is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.

MED-ALL-PTC923-2500012 | September 2025

This symposium was developed and funded by PTC Therapeutics for SSIEM 2024.

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MED-ALL-PKU-2400224 | October 2025

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