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Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Congress activities | International Congress on Neuromuscular Diseases (ICNMD) | ICNMD 2024 presentation: Age at loss of ambulation in patients with nmDMD from the STRIDE Registry: Sensitivity analyses

ICNMD 2024 presentation: Age at loss of ambulation in patients with nmDMD from the STRIDE Registry: Sensitivity analyses

The ICNMD 2024 presentation explored whether other sources of bias were adequately controlled in evaluating ataluren plus standard of care (SoC) on loss of ambulation for patients in the STRIDE Registry

  • Learn more about the reliability of the use of ataluren in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD)
  • Understand how propensity score matching methodology was performed in the STRIDE Registry and CINRG DNHS
  • Assess whether potentially important sources of bias were adequately controlled in assessing the efficacy of ataluren plus SoC on loss of ambulation in STRIDE Registry patients
▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.

MED-ALL-ATLN-2500006 | September 2025

This symposium was developed and funded by PTC Therapeutics for ICNMD 2024.

The information in the materials was correct at the time of the events.

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MED-ALL-DMD-2500001 | June 2025

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