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Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Congress activities | International Congress on Neuromuscular Diseases (ICNMD) | ICNMD 2024 symposium: Spotlight on nmDMD exploring a targeted treatment option

ICNMD 2024 symposium: Spotlight on nmDMD exploring a targeted treatment option

This symposium, presented at ICNMD 2024, provides an overview of clinical trial and real-world data for nonsense mutation Duchenne muscular dystrophy (nmDMD) and highlights the importance of continuous care

  • Understand the developmental timeline of ataluren
  • Review clinical and real-world evidence for ataluren in patients with nmDMD 
  • Appreciate the importance of continuous care through real-world case studies
▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.

MED-ALL-ATLN-2500006 | September 2025

This symposium was developed and funded by PTC Therapeutics for ICNMD 2024.

The information in the materials was correct at the time of the events.

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MED-ALL-DMD-2500001 | June 2025

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MED-ALL-CORP-2200029 | June 2025

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