MDA 2020 poster: Pulmonary function in non-ambulatory patients with nonsense mutation Duchenne muscular dystrophy (nmDMD) from the STRIDE ataluren Registry and CINRG Duchenne Natural History Study: A matched cohort analysis
View a comparison of pulmonary function decline in matched cohorts of Duchenne muscular dystrophy (DMD) patients in our poster presented at MDA 2020
Pulmonary function data from two international registries: propensity-score matched analyses of non-ambulatory patients with nmDMD receiving a mutation-specific DMD therapy plus standard of care (SoC; corticosteroid or palliative therapies; data cut-off: 31 January 2019) and non-ambulatory DMD patients receiving SoC alone are presented
Kaplan-Meier estimates of the age at loss of ambulation and pulmonary functional decline in each cohort are included
▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC at firstname.lastname@example.org.
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