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Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Publications | Publication: Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD): Patient demographics and characteristics from the STRIDE Registry

Publication: Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD): Patient demographics and characteristics from the STRIDE Registry

This research article, published in the Journal of Comparative Effectiveness Research, outlines the initial demographics and baseline characteristics of patients enrolled in Strategic Targeting of Registries and International Database of Excellence (STRIDE), an observational registry of nmDMD patients receiving a mutation-specific DMD therapy

  • The demographics and baseline characteristics of the STRIDE Registry population and the principal interim safety results (data cut-off: 9 July 2018) is presented
▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.

MED-ALL-ATLN-2500006 | September 2025

Muntoni F, Desguerre I, Guglieri M, et al. J Comp Eff Res. 2019;8(14):1187–1200

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MED-ALL-DMD-2200190 | June 2025

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