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Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Publications | Publication: Duchenne muscular dystrophy management and treatment access challenges: Case report

Publication: Duchenne muscular dystrophy management and treatment access challenges: Case report

Published in the New Emirates Medical Journal, this case report discusses the challenges of treatment access and meeting Duchenne muscular dystrophy (DMD) care guidelines in the Middle East in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD)

  • Learn about the challenges of caring for patients with nmDMD in the Middle East
  • Review the effectiveness of the first use of ataluren in patients with nmDMD in this region
  • Understand the impact of timely diagnosis and management in patients with nmDMD
▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC Therapeutics at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally; always consult local prescribing information and/or Summary of Product Characteristics before prescribing any products.

MED-ALL-ATLN-2500006 | September 2025

El-Azzabi TI. New Emir Med J. 2023;4(1)

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MED-ALL-DMD-2300173 | June 2025

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