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Publication: Prednisone and deflazacort in Duchenne muscular dystrophy: A patient perspective and plain language summary publication of the Cincinnati study

This article in the Journal of Comparative Effectiveness Research summarizes the Cincinnati study, which investigated the effectiveness of 2 corticosteroid treatments in prolonging motor function in Duchenne muscular dystrophy (DMD)

  • Explore the outcomes from the Cincinnati study
  • Learn about the background and demographics of the 435 boys with DMD who took part in the study
  • Compare patient outcomes to understand the differences between 2 corticosteroid treatments

Wong BL, Cook T, Miller H. J Comp Eff Res. 2022;11(11):779–786

Deflazacort is a corticosteroid indicated for the treatment of Duchenne muscular dystrophy (DMD) in patients 2 years of age and older. PTC Therapeutics is the Marketing Authorization Holder for deflazacort in the US only. Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The US Prescribing Information for deflazacort is available here. Please refer to your local country guidance for more information.

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