Home | Neuromuscular | Duchenne muscular dystrophy (DMD) | Publications | Publication: Real-world outcomes of long-term prednisone and deflazacort use in patients with Duchenne muscular dystrophy: Experience at a single, large care center

Publication: Real-world outcomes of long-term prednisone and deflazacort use in patients with Duchenne muscular dystrophy: Experience at a single, large care center

This research article, published in the Journal of Comparative Effectiveness Research, provides results from a retrospective real-world analysis of corticosteroid use in patients with Duchenne muscular dystrophy (DMD)

Find out about the background and demographics of the 435 boys included in this retrospective, real-world analysis
Read more about the comparison between clinical outcomes of corticosteroid treatments for DMD, as assessed by median age at loss of ambulation, incidence of scoliosis, lean body mass, stature, and weight
Review a cross-sectional analysis of the outcomes to further understand associations between steroid type and patient status

PTC Therapeutics is the Marketing Authorization Holder for deflazacort in the US only. Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The US Prescribing Information for deflazacort is available here. Please refer to your local country guidance for more information.

For medical information, product complaints, or to report an adverse event, please call 1-866-562-4620 or email at usmedinfo@ptcbio.com. You may also report adverse events directly to FDA at 1-800-FDA-1088 or www.fda.gov/medwatch.

MED-ALL-DFZ-2500002 | March 2025

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MED-ALL-DMD-2200118 | June 2025

Publication: Real-world outcomes of long-term prednisone and deflazacort use in patients with Duchenne muscular dystrophy: Experience at a single, large care center

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