MDA 2022 poster: Age at loss of ambulation in patients with DMD from the STRIDE Registry and the CINRG Natural History Study: A matched cohort analysis

This poster, from the 2022 MDA Conference in Nashville, Tennessee, USA, compares the age at loss of ambulation in patients with nonsense mutation Duchenne muscular dystrophy (nmDMD) enrolled in the STRIDE Registry and CINRG Natural History Study

• Explore the demographics, including corticosteroid use, of propensity score-matched patients who either received a mutation-specific treatment for nmDMD plus standard of care (SoC), or received SoC alone
• Review Kaplan-Meier analyses used to evaluate the difference in median age at loss of ambulation between the 2 cohorts

▼ Ataluren is subject to additional monitoring. This will allow quick identification of new safety information. Healthcare professionals are asked to report any suspected adverse reactions via the national reporting system. Adverse events should also be reported to PTC at pharmacovigilance@ptcbio.com.

Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The European Summary of Product Characteristics for ataluren is available here. Please refer to your local country guidance for more information.

Deflazacort is a corticosteroid indicated for the treatment of Duchenne muscular dystrophy in patients 2 years of age and older. PTC Therapeutics is the Marketing Authorization Holder for deflazacort in the US only. Registration conditions differ internationally, and prescribing information may vary depending on local approval in each country. The US Prescribing Information for deflazacort is available here. Please refer to your local country guidance for more information.

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